Category:
About the Event
Join the Department of Neurology for a presentation by Neil Aronin, M.D., FACP, titled “Advances in Molecular Therapy for Huntington’s Disease.” Aronin is division chief of endocrinology and metabolism at the University of Massachusetts Medical School.
Email Michele Davis for the Zoom information.
Objectives
By the end of this presentation, the audience participant should be able to:
- Understand molecular therapies for treatment of a mutant gene that causes neurodegenerative disease.
- Describe two different approaches to reduce the mutant mRNA: small interfering RNA and microRNA in a virus.
- Edit the mutant gene to inactivate it or to correct it